Highly effective treatments for HIV keep people healthy, but we do not yet have a safe and scalable way to completely rid the ...

StitchR makes it possible to deliver larger payloads with current vectors, expanding the list of diseases targetable by gene therapies.

StitchR, a new gene therapy technique, delivers large genes in two parts to treat muscular dystrophies by restoring critical proteins in animal models.

Gene therapy can effectively treat various diseases, but for some debilitating conditions like muscular dystrophies there is a big problem: size.

CRISPR-Cas9 is a powerful gene-editing tool that allows scientists to modify DNA in living organisms precisely. It works like ...

Gene therapy can effectively treat various diseases, but for some debilitating conditions like muscular dystrophies there is a big problem: size. The ...

Life Sciences Center (LSC) have discovered a unique way for cells to silence specific genes without cutting DNA. This ...

A research team led by Professor Lee Sang-hwa of the Synthetic Biology Project Group of the Catholic Central Medical Center's ...

CRISPR gene editing can have unforeseen consequences on the structure of chromosomes, says the University of Zurich.

The CRISPR tool is capable of repairing the genetic defect responsible for the immune disease chronic granulomatous disease. However, researchers have now shown that there is a risk of inadvertently ...

The CRISPR molecular scissors have the potential to revolutionize the treatment of genetic diseases. This is because they can ...